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  • News bot April 28, 2026, 11:35 a.m.

    📋 ROCKET PHARMACEUTICALS, INC. (RCKT) - Clinical Trial Update

    Filing Date: 2026-04-28

    Accepted: 2026-04-28 07:34:42

    Event Type: Clinical Trial Update

    Event Details:

    ROCKET PHARMACEUTICALS, INC. (RCKT) Announces Clinical Trial Update ROCKET PHARMACEUTICALS, INC. (RCKT) provided an update on its clinical development programs. Clinical Development Highlights:
    • Diseases/Conditions: $180 million
    • Collaboration: Rocket Pharmaceuticals

    🔬 Clinical Development Pipeline (ROCKET PHARMACEUTICALS, INC.):

    Product Type Development Stage Therapeutic Area Source
    RP-L301 Other Phase PHASE2 Pyruvate Kinase Deficiency ClinicalTrials.gov
    RP-A601 Other Phase PHASE1 PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) ClinicalTrials.gov
    no intervention OTHER Preclinical Neonatal Acute Respiratory Distress Syndrome(ARDS) ClinicalTrials.gov
    SIS-reinforced anastomosis DEVICE Phase PHASE4 Rectal Cancer ClinicalTrials.gov
    RP-A701 is a recombinant viral vector composed of an AAV serotype rh.74 (AAVrh.74) capsid encapsulating the transgene, BCL2-associated Athanogene 3 (BAG3) GENETIC Phase PHASE1 Dilated Cardiomyopathy (DCM) ClinicalTrials.gov
    RP-A501 GENETIC Phase PHASE2 Danon Disease ClinicalTrials.gov
    Cardiac Assistive Device DEVICE Preclinical Danon Disease ClinicalTrials.gov
    Heart Transplant PROCEDURE Preclinical Danon Disease ClinicalTrials.gov
    RP-L401 BIOLOGICAL Phase PHASE1 Infantile Malignant Osteopetrosis ClinicalTrials.gov
    Safety and efficacy assessments OTHER Preclinical Fanconi Anemia Complementation Group A ClinicalTrials.gov
    RP-L102 BIOLOGICAL Phase PHASE2 Fanconi Anemia Complementation Group A ClinicalTrials.gov
    RP-L201 BIOLOGICAL Phase PHASE1 Leukocyte Adhesion Defect - Type I ClinicalTrials.gov

    💼 Business Developments:

    • Partnership
    • Acquisition
    • Licensing: Not available
    • Regulatory Approval
    • Executive Changes: Not available

    Structured Data:

    • Company Name: ROCKET PHARMACEUTICALS, INC.
    • Ticker Symbol: RCKT